These Data Highlight Unmet Medical Need for Therapies to Control Phe Concentrations by Targeting the Underlying Cause of PKU BEDFORD, Mass., Dec. 16, 2019 (GLOBE NEWSWIRE) -- Homology Medicines, Inc. ...
BEDFORD, Mass., July 27, 2023 (GLOBE NEWSWIRE) -- Homology Medicines, Inc. (Nasdaq: FIXX), a genetic medicines company, announced today encouraging initial clinical data from the first dose cohort in ...
Findings showed pegvaliase reduced mean blood Phe levels from baseline by 49.7% compared with 0.3% with diet only at week 72.
People with phenylketonuria cannot break down a substance in food called phenylalanine. Following a phenylketonuria diet is the main treatment for preventing serious symptoms. People with ...
GAINESVILLE, Fla. -- A breakdown in brain cell communication may contribute to the most common biochemical cause of mental retardation, University of Florida scientists have discovered. The process is ...
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