Picture CRISPR-Cas9, a gene editing technology, as a GPS-guided scalpel: gRNA directs the Cas9 enzyme, a protein that cuts ...

Sickle cell disease is caused by a single genetic mutation that alters the shape of red blood cells. While the condition ...

NHS Scotland has approved a one-time CRISPR gene therapy for severe sickle cell disease, offering durable reduction in vaso-occlusive crises for eligible patients.

GLP-1 receptor agonist use appeared linked to significantly reduced all-cause mortality among people with sickle cell disease ...

Why Elon Musk says saving for retirement will be 'irrelevant' in the next 20 years Welcome to Greenland, an economy reliant on subsidies and shrimp 17 college basketball players charged in ...

ANN ARBOR, Mich. (WJRT) - A Saginaw family is celebrating the new year at Mott Children's Hospital as their son, 10-year-old Elijah Dottery, continues his fight against sickle cell anemia. He was ...

A year ago, NBC News joined Wedam Minyila as he began undergoing a groundbreaking treatment for sickle cell disease. The ...

Medicaid is doing a novel payment system for the new, promising and expensive sickle cell treatment. It may become a model ...

Caring Cross, a 501(c)(3) non-profit dedicated to improving access to advanced therapies, and Boston Children's Hospital today announced a collaboration to provide a sustainable, affordable pathway ...

NEW YORK – Boston Children's Hospital has granted a worldwide license for an investigational gene therapy for sickle cell disease and beta thalassemia to Caring Cross, the nonprofit announced this ...

CS-101 is Shanghai-based CorrectSequence's lead candidate, which it is developing for treating sickle-cell disease and ...